Table 2 of Prommajan, Mol Vis 2011; 17:456-460.
Constructs |
α-L-iduronidase activity (nmol/h/mg cell protein) mean±SD |
Phenotype |
---|---|---|
None | 27.17±4.89 | - |
pEFNeo | 32.52±10.58 | - |
pEFNeo/IDUA | 435.04±56.23 | - |
pEFNeo/p.W402X | 21.10±12.57 | Hurler |
pEFNeo/p.E276K | 31.88±6.05 | Scheie |